Speakers

Mayor of Athens

Vice President, European Parliament

Chief Executive Officer, EURORDIS-Rare Diseases Europe

President, Hellenic Association of Pharmaceutical Companies (SFEE) & General Manager, Novo Nordisk Hellas

President EAE, Founder & Chair of 'Positive Voice'

President “95” Rare Alliance Greece, EUPATI

Professor, Director of LabHEM, University of Piraeus, Department of Economics

Alternate Minister of Health, Ministry of Health, Greece
Minister for Labor & Social Affairs, Greece

CEO of the Institute of Pharmaceutical Research And Technology (IFET)

Head Value Access, Health Policy & RWE, IQVIA Hellas

President, EODY Professor of Pediatrics NKUA

Prof of Genetics, NKUA, Director Laboratory of Medical Genetics, St. Sophia's Children's Hospital, Athens, Greece
MD, PhD, FMH (CH) Prof. of Pediatrics-Pediatric Endocrinology, Director First Dept Pediatrics Medical School NKUA

Inborn Errors of Metabolism, Dept of Pediatrics & Adolescent Medicine, Med. Univ. Vienna

PgCert MSc PhD, Clinical Geneticist- Paediatrician, Medical Genetic Unit

Deputy Head of the Autonomous Department of Therapeutic Protocols & Patient Registries, Ministry of Health

Deputy Head of the Autonomous Department of therapeutic Protocols & Patient Registries, Ministry Of Health

Director of the Office of the Minister of Digital Governance

MD, MSc Public Health, General Practitioner, Greek NHS Consultant, Director, Quality Improvement of Health Services

Professor of Pediatric Hematology-Oncology, President, Hellenic Society of Pediatric Hematology-Oncology

MD, PhD Cardiologist, Deputy Director of the Cardiology Department, Onassio Cardiac Surgery Center

MD, PhD, Emeritus Prof. Medical Faculty, Aristotle Univ. Thessaloniki, Chairman “KRIKOS ZOIS”, Member EB RDG

Prof. of Cardiology, Athens Medical School, A' Cardiology Clinic, Athens Univ., 'HIPPOCRATIO' Gen. Hospital Of Athens

MD, PhD, FIDSA, FAAM, FESCMID Prof. of Paediatrics – Infectious Diseases, Aristotle Univ. School of Medicine

MD, PhD, MPH Committee for orphan Medicinal Products (COMP) Chair, European Medicines Agency (EMA)

Secretary General, European Confederation of Pharmaceutical Entrepreneurs (EUCOPE)

Paediatric Referent ANSM, Vice-chair & French Delegate of the Paediatric Committee, EMA

Executive Director, Global Regulatory Affairs – Development Strategy, Alexion International

Alternate Member of the Committee for Advanced Therapies, EMA, Trustee at FundAME, Spanish Delegate at SMA Europe

Head of Government Affairs & Public Policy for EMEA & Asia Pacific Region, PTC Therapeutics

Psychiatrist, Member of The European Parliament

Head of Patient Advocacy, Global Product Development, Pfizer Rare Disease

EJP RD Coordinator, Assistant Director, Thematic Institute of Genetics, Genomics & Bioinformatics, INSERM, France

Associate Professor, Department of Biomedical, Metabolic & Neurosciences Ex-Sc. Biomedical, UNIMORE

ERICA Project Manager

Executive Director, Science Policy & Regulatory Affairs At EFPIA

Pharmacoepidemiologist and RWE specialist within the Data Analytics and Methods Taskforce at EMA

Special Adviser, Lead Methodologist in Regulatory & Pharmacoeconomic Statistics, NoMA, Teamleader iHTA, NoMA

Coordinator of the Orphanet Work Direct Grant & of the RD-CODE Project

Professor of Psychiatry at University of Miami & Professor of Pharmacology at Università Di Modena E Reggio Emilia

PhD Senior Policy Officer- Research Programmes Rare Diseases, Health Data, Artificial Intelligence, European Commission

Head of Research & Development, Global Rare Diseases, Chiesi

Senior Policy Advisor, World Health Organization (WHO Europe)

PharmD (a. I.) Head of Advanced therapies Office & Oncology RA, Senior Specialist Human Medicines Division, EMA

MEP, EPP Group in the European Parliament

President European Haemophilia Consortium, PRAC Member

Scientific Officer, Project Leader at the European Commission Directorate General Joint Research Centre

Chair International Alliance of Patients' Organizations, President, Canadian Organization for Rare Disorders (DORD

A Vice Pres. RDG, C Vice Pres. Greek Patient Association, Pres. Cancer & RD Association Evros „Together for Life“

President HTA Committee, Associate Professor of Pediatrics – Adolescent Medicine, NKUA

Ass. Professor at NKUA President of the National Organization for Medicines (EOF)

Co-Founder NGO Karkinaki, Awareness for Childhood & Adolesccent Cancer

General Secretary of Primary Care Services, Ministry of Health, Greece

President at Greek Lysosomal Association
Scientific Officer, Europ.Commission, Joint Research Centre, Directorate F – Health & Food, JRC.F1 - Disease Prevention

Director of The Department of Rare Skeletal Diseases, Rizzoli Orthopaedic Institute
Assistant Professor, Institute of Neurology, Department of Neuropathology and Neurochemistry, MedUni Vienna

President Rare Diseases Greece, EMA Pediatric Committee, EPF, WDO, EAE Board Member

Director General, European Federation of Pharmaceutical Industries And Associations (EFPIA)
MEP, Member of the Committee on the Environment, Public Health and Food Safety (ENVI), (TRAN) & (COVI)

Global Access Strategy Lead for Rare Diseases, Neuroscience & Gene Therapies. Roche
Prof. of Obstetrics -Gynaecology Fetomaternal Medicine, Hippokrateion General Hosp. Aristotle Univ. Thessaloniki
DG SANTE, European Commission
Industry

Executive Director, Thalassaemia International Federation (TIF)
Senior International Affairs Officer, Thalassaemia International Federation
Policy Officer, European Commission Directorate-General for Health and Food Safety Unit B3, ERNs
Booths

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